Setmelanotide
Setmelanotide (Imcivree)
Evidence & Status
- FDA Approved
- Strong Human Evidence
- Strong
FDA Approval Scope
Current U.S. labeling: POMC, PCSK1, or LEPR deficiency and Bardet-Biedl syndrome for patients age 2 years and older; acquired hypothalamic obesity for patients age 4 years and older.
At a Glance
A cyclic octapeptide MC4R agonist with label-specific U.S. indications and age boundaries.
Plain English
Setmelanotide is used only within its current product-label scope; it is not a general treatment for common or polygenic obesity.
Overview
A cyclic octapeptide MC4R agonist. Current U.S. labeling includes POMC, PCSK1, or LEPR deficiency and Bardet-Biedl syndrome for patients age 2 years and older, and acquired hypothalamic obesity for patients age 4 years and older. This record does not generalize those indications to common or polygenic obesity.
Research Summary
Direct Phase 3 human evidence includes POMC/PCSK1/LEPR-deficiency obesity and Bardet-Biedl syndrome populations. Administration, pharmacokinetics, and safety remain product- and label-specific.
Research Areas
- Genetic & hypothalamic obesity (POMC/PCSK1/LEPR deficiency, BBS, acquired HO)
- MC4R pathway physiology
- Hypothalamic obesity
- Melanocortin signaling
Safety & Risks
Serious Risks
- Depression and suicidal ideation have occurred; monitor for new or worsening depression, suicidal thoughts, or suicidal behavior
- Serious hypersensitivity reactions, including anaphylaxis, have been reported; prior serious hypersensitivity to setmelanotide or IMCIVREE excipients is a formal contraindication
- Generalized skin hyperpigmentation, darkening of existing nevi, and development of new melanocytic nevi can occur; full-body skin examination is recommended before treatment and periodically during treatment
- Spontaneous penile erections and other sexual adverse effects can occur; erections lasting longer than 4 hours require urgent medical attention
- Patients with acquired hypothalamic obesity require monitoring for acute adrenal insufficiency
- Patients with acquired hypothalamic obesity and central diabetes insipidus require monitoring for sodium imbalance, including hyponatremia and hypernatremia
Reported Side Effects
- Skin hyperpigmentation
- Injection site reactions
- Nausea
- Headache
- Diarrhea
- Abdominal pain
- Vomiting
- Depression
- Spontaneous penile erection
Legal Status by Region
- United States
- FDA-approved only for current labeled indications; not generalized to common or polygenic obesity.
- United Kingdom
- EMA-approved
- Australia
- TGA-approved
- Canada
- Health Canada-approved
Citations & Sources
- Efficacy and safety of setmelanotide, an MC4R agonist, in individuals with severe obesity due to LEPR or POMC deficiency: single-arm, open-label, multicentre, phase 3 trials
2020
PMID 33137293
- Efficacy and safety of setmelanotide, a melanocortin-4 receptor agonist, in patients with Bardet-Biedl syndrome and Alström syndrome: a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial with an open-label period
2022
PMID 36356613
- IMCIVREE (setmelanotide) injection — Prescribing Information
2026
Regulatory NDA 213793